Meaningful gains in skills seen with Rett gene therapy in trial: Data
The first four Rett syndrome patients treated with the gene therapy candidate NGN-401 have seen meaningful gains in skills, data show.| Rett Syndrome News
Newron Pharmaceuticals stopped work on sarizotan in May 2020 after it failed to show superiority to placebo in treating breathing problems in Rett patients.| Rett Syndrome News
The first four Rett syndrome patients treated with the gene therapy candidate NGN-401 have seen meaningful gains in skills, data show.| Rett Syndrome News
Category archive page for News.| Rett Syndrome News
Learn more about the rare neurodevelopmental disorder Rett syndrome, including its causes, symptoms, diagnosis and treatment.| Rett Syndrome News
