Gaucher Disease Type 3 (GD3) is a rare lysosomal storage disorder characterized by both visceral and neurological involvement. Pulmonary manifestations can s...| Frontiers
Learn about the various symptoms of Gaucher disease, including those that are bone- or organ-related, and neurological symptoms.| Gaucher Disease News
Enzyme replacement therapy (ERT) is a key treatment approach for Gaucher disease that addresses the underlying cause of the genetic disorder.| Gaucher Disease News
October 13, 2025| Gaucher Disease News
FLT201, a gene therapy for Gaucher disease type 1, led to sustained increases in enzyme levels in animal models, a study showed.| Gaucher Disease News
Gaucher disease is a genetic disorder that can cause enlarged organs, blood disorders, bone abnormalities, and neurological complications.| Gaucher Disease News
