A gene therapy showing potential to restore lost developmental milestones in people living with Rett syndrome has earned breakthrough therapy status from the U.S. Food and Drug Administration (FDA). The experimental therapy, TSHA-102, is being developed by Taysha Gene Therapies. A breakthrough therapy designation is intended to speed the development and review of important new treatments for […] The post FDA grants breakthrough status to Rett syndrome treatment appeared first on Rett Synd...| Rett Syndrome News – The Web's Daily Resource for Rett Syndrome News
Columnist Jacqueline Babiarz reflects on the passing of her 14-year-old daughter, Cammy, due to complications from Rett syndrome.| Rett Syndrome News
Approved in the U.S. in March 2023, Daybue (trofinetide) is a daily treatment for Rett syndrome that can be taken by mouth or feeding tube.| Rett Syndrome News
Marisa Wexler is a senior science writer for Rett Syndrome News with an MS in cellular and molecular pathology. She covers the latest news and information on a variety of Rett syndrome topics.| Rett Syndrome News
Category archive page for News.| Rett Syndrome News
Learn more about the rare neurodevelopmental disorder Rett syndrome, including its causes, symptoms, diagnosis and treatment.| Rett Syndrome News