Children with Fragile X share traits with those with autism spectrum disorder, but show differences in brain network patterns, per a study.| Fragile X News Today
SPG601, an oral treatment for fragile X syndrome that's now in clinical testing, has been granted orphan drug status in the European Union.| Fragile X News Today
The FDA has granted orphan drug and rare pediatric disease designations to fragile X treatment KER-0193, Kaerus Biosciences said.| Fragile X News Today
Long-term treatment with ZYN002 cannabidiol gel eased symptoms of irritability in children and adolescents with fragile X syndrome, per trial data.| Fragile X News Today
Kaerus is planning a proof-of-concept Phase 2 trial for KER-0193 after its fragile X syndrome treatment was found safe in healthy adults.| Fragile X News Today
The FDA granted fast track designation to Spinogenix's experimental oral therapy SPG601 to treat fragile X syndrome.| Fragile X News Today
Zygel safely led to behavioral improvements among children with fragile X syndrome, including those likely to have severe disease.| Fragile X News Today
Findings from researchers in Canada and Maryland support further development of gene therapy for treating people with fragile X syndrome.| Fragile X News Today
The International Fragile X Premutation Registry, which aims to speed research into the impact of premutations, is enrolling participants.| Fragile X News Today
The Canadian government has cleared KGK Science's Phase 2a trial testing NM-1001, a psilocybin microdose therapy, in fragile X syndrome.| Fragile X News Today
Tetra Therapeutics’ investigational oral therapy BPN14770 safely and effectively improved cognitive function in men with fragile X syndrome.| Fragile X News Today
A U.S. study shows that repeated sampling of hair follicles in people with fragile X syndrome can be used to measure FMRP protein levels.| Fragile X News Today
Due to the variability of its symptoms, a conclusive diagnosis of fragile X syndrome can only be obtained with genetic testing.| Fragile X News Today
Read about the characteristic symptoms of fragile X syndrome, which range from developmental and behavioral problems to physical features.| Fragile X News Today
Children with fragile X syndrome have had problems with their academic performance and social interactions since the COVID-19 pandemic.| Fragile X News Today
Fragile X syndrome is caused by low to no levels of the FMRP protein, important for brain development, due to mutations in the FMR1 gene.| Fragile X News Today
Tetra Therapeutics has amended the protocols of two ongoing clinical trials testing zatolmilast to improve access for fragile X patients.| Fragile X News Today
The International Fragile X Conference in July will bring together patients, caregivers, and professionals to learn about fragile X research.| Fragile X News Today
The FDA has approved a Phase 2 trial to test SPG601, an oral treatment candidate, in men with fragile X syndrome.| Fragile X News Today
The LivJoy Foundation is funding a four-year postdoctoral fellowship for a scientist at USC who will study fragile X syndrome in females.| Fragile X News Today
A combination of ibudilast and gaboxadol was shown to normalize behavior and improve memory in a mouse model of fragile X syndrome.| Fragile X News Today
Blood levels of two proteins, known as MMP9 and APP, could serve as biomarkers for fragile X syndrome where genetic testing is not possible.| Fragile X News Today
Fragile X-causing mutations in FMR1 cause structural DNA changes that affect other genes necessary for nerve cell function, a study says.| Fragile X News Today
School age-girls with fragile X show significantly poorer cognitive function and academic performance relative to matched healthy girls.| Fragile X News Today
Sensory symptoms, including overreactions to stimuli, are very common among fragile X patients and affect their daily life, a study found.| Fragile X News Today
Experimental blarcamesine (Anavex 2-73) was able to slow cognitive and functional decline in early Alzheimer’s patients over a year, data show.| Alzheimer's News Today