Pivotal NGN-401 trial speeds toward dosing for people with Rett
NGN-401, a gene therapy treatment people with Rett syndrome, has shown positive results from an ongoing Phase 1/2 trial.| Rett Syndrome News
NGN-401, a gene therapy treatment people with Rett syndrome, has shown positive results from an ongoing Phase 1/2 trial.| Rett Syndrome News
Neurogene received clearance from the FDA for a pivotal trial of NGN-401, which could support an application for the gene therapy's approval.| Rett Syndrome News
NLX-101 improves breathing issues and cognitive function in a female mouse model of Rett syndrome, a study showed.| Rett Syndrome News
On the anniversary of her oldest daughter's death, columnist Jacqueline Babiarz has cried herself to sleep remembering those last 24 hours.| Rett Syndrome News
