Exciting progress on a new approach treating Nemaline Myopathy! Dr. Afrooz Rashnonejad is developing a gene therapy for ACTA1-related NM/NEM3.| A Foundation Building Strength
Meet our team of scientists, researchers and doctors dedicated to advancing research for Nemaline Myopathy.| A Foundation Building Strength
Promising news! Gene therapy research for Nemaline Myopathy (NEM3) progresses with successful pre-clinical trials in mice. Learn more about Dr. Rashnonejad's innovative approach and its potential to offer hope for NEM3 patients.| A Foundation Building Strength