Gaucher disease gene therapy FLT201 shows proof of concept
FLT201, a gene therapy for Gaucher disease type 1, led to sustained increases in enzyme levels in animal models, a study showed.| Gaucher Disease News
FLT201, a gene therapy for Gaucher disease type 1, led to sustained increases in enzyme levels in animal models, a study showed.| Gaucher Disease News
Treatment with a corticosteroid and hydroxychloroquine eased symptoms of severe lung problems in an infant with type 3 Gaucher disease.| Gaucher Disease News
