Blocking a small RNA molecule that helps control whether certain genes are switched on or off reactivated the healthy copy of the MECP2 gene in a mouse model of Rett syndrome, increasing lifespan and activity, and improving breathing. While blocking miR‑106a appears to be “a feasible therapeutic strategy,” before it can be advanced to clinical […] The post Gene therapy ‘sponge’ revives healthy gene in Rett syndrome appeared first on Rett Syndrome News.
