Gaucher disease gene therapy FLT201 shows proof of concept
FLT201, a gene therapy for Gaucher disease type 1, led to sustained increases in enzyme levels in animal models, a study showed.| Gaucher Disease News
Enzyme replacement therapy (ERT) is a key treatment approach for Gaucher disease that addresses the underlying cause of the genetic disorder.| Gaucher Disease News
FLT201, a gene therapy for Gaucher disease type 1, led to sustained increases in enzyme levels in animal models, a study showed.| Gaucher Disease News
Columnist Rivka Silver has found that strength training with Pilates has been the exercise that works best to relieve her inflammation.| Gaucher Disease News
Treatment with a corticosteroid and hydroxychloroquine eased symptoms of severe lung problems in an infant with type 3 Gaucher disease.| Gaucher Disease News
